Skip to content

Legislative Life Science Caucus

Life Sciences Caucus Documents

2022 Meetings

June 28, 2022 Rare Diseases and Gene Therapy

Gene therapy and rare diseases topic of Life Sciences Caucus

The General Assembly's Life Sciences Caucus met Tuesday, June 28, to learn about the promise of gene therapies as potential treatments for rare diseases.

Nearly two dozen legislators and staff members heard from Priya Kishnani, M.D., and Vandana Shashi, M.D., of the Duke Undiagnosed Diseases Network and Marianne Hamilton Lopez, M.D., of the Duke Margolis Center for Health Policy along with Charlene Cowell, executive director of Bleeding Disorders of North Carolina. Caucus Co-Chairs Sen. Paul Newton, Sen. Mike Woodard and Rep. Donna White were in attendance.

Hamilton Lopez told legislators that gene therapies will often differ from traditional treatment in that the therapies may only be administered once as opposed to conventional treatments that are given as multiple or continual doses of medication. Gene therapies are currently much more expensive than conventional therapies, which makes them a challenge for our current system to pay. The upfront cost of these breakthrough therapies must be weighed against the impressive benefits they offer compared to conventional therapies.

Presentation

Story of Wade Hosey, child with spinal muscular atrophy

Sen. Paul Newton and Rep. Donna White, Life Science Caucus Meeting, June 27 2022

Caucus Co-Chairs Sen. Paul Newton and Rep. Donna White

Caucus Co-Chair Sen. Mike Woodard

Caucus Co-Chair Sen. Mike Woodard

Life Sciences Caucus Meeting, June 27, 2022

Feb. 23, 2022 Tour of NC Reseach Campus

2021 Meetings

2020 Meetings

October 19, 2020 Virtual Meeting
September 14, 2020 Virtual Meeting
May 19, 2020 Virtual Meeting
March 10, 2020 Lee County Tour
February 3, 2020 Johnston County Tour

2019 Meetings

2018 Meetings

NC Life Sciences Headlines

Eli Lilly breaks ground on $1 billion NC campus

Global pharma opens $100 million facility as Sanford boom continues

Nash County set for economic expansion as Raleigh-based SinnovaTek buys, builds facility

California startup opening RTP facility, hiring on heels of $68 million raise
Drug giant Eli Lilly to build new $1 billion plant in Concord, create nearly 600 jobs

West Pharmaceutical investing additional $70M, will add 70+ jobs in Kinston

Winston-Salem hosts space station builder's regenerative medicine accelerator

Triad startup raises $30 million, to add 200 jobs

New $18 million agriculture research facility coming to RTP

Biotech to expand Triangle footprint with new manufacturing site in Morrisville

Wilmington CRO expands globally through European acquisition
Genetics firm launches tests for children

Stem cell firm launching Durham facility to attract business

Winston-Salem's Novex Innovations growing rapidly

Cancer diagnostics firm to add jobs as it expands
Alcami to invest $10 million, hire 40, in Durham

Agtech GreenLight is growing presence in RTP

Drug giant Fujifilm Diosynth adding more jobs, expanding plant

Wilmington's Alcami buys Massachusetts company

Marrone Bio Innovations will move HQ to NC

Massive $1 billion biotech campus being planned for Morrisville

Life science campus coming to Holly Springs

Genetics firm launches tests for children

Bioventus completes acquisition of Israeli firm CartiHeal

Stem cell firm launching Durham facility to attract business

Winston-Salem's Novex Innovations growing rapidly

Cancer diagnostics firm to add jobs as it expands

Genetics firm launches tests for children

Stem cell firm launching Durham facility to attract business

Winston-Salem's Novex Innovations growing rapidly

Cancer diagnostics firm to add jobs as it expands